Lipidoses - 55 Studies Found
Recruiting |
: International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV) and Related Diseases : Neutral Lipid Storage Disease : 2016-08-04 |
Completed |
: The Effect of Fibrate Therapy in Two Patients With Neutral Lipid Storage Disease With Myopathy (NLSDM) : Neutral Lipid Storage Disease : 2012-01-16 : Drug: Fibrate treatment Patients will receive a dosage of 400mg Bezafibrate every day during 28 weeks |
Recruiting |
: Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2014-11-07 : Drug: Olipudase alfa Pharmaceutical form: powder for concentrate for solution for infusion Route of admi |
Recruiting |
: A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2013-11-26 : Drug: GZ402665 Pharmaceutical form: Powder for concentrate |
Recruiting |
: Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2013-11-26 :
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Recruiting |
: Clinical Study on the Safety of CNT-02 for TGCV and NLSD-M :
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Recruiting |
: Study of Inborn Errors of Cholesterol Synthesis and Related Disorders : Lipoidosis : 2002-09-21 |
Completed |
: SCH-58235 (Ezetimibe) to Treat Homozygous Sitosterolemia : Lipoidosis : 2002-09-10 : Drug: SCH-58235 |
Recruiting |
: International Collaborative Gaucher Group (ICGG) Gaucher Registry :
: Drug: Cerezyme (imiglucerase for injection) |